Adenine Base Editors: A Novel Approach to Treat CLN2 Disease (127780)
Jill M Weimer
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Mitchell J Rechtzigel
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,
Peyton E Randolph
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,
Gregory Newby
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,
Clarissa D Booth
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,
Melissa A Pratt
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,
Hannah G Leppert
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,
Joelle T Anderson
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,
Kaylie J Timm
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,
David R Liu
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- Sanford Health Research, Sioux Falls, South Dakota, United States
- Sanford School of Medicine at University of South Dakota, Vermillion, South Dakota, United States
- Broad Institure of MIT and Harvard, Cambridge, MA, United States
- Harvard Medical School, Boston, MA, United States